통합검색
내가 찾은 검색어
'hemophilia A' 에 대한 통합검색결과 19건입니다.
한빛사19건
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Long-term correction of hemophilia A via integration of a functionally enhanced FVIII gene into the AAVS1 locus by nickase in patient-derived iPSCs
- Exp. Mol. Med. 06 January 2025 | https://doi.org/10.1038/s12276-024-01375-z
- 2025.01
- 의약학
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박철용
연세대학교 의과대학, 에스바이오메딕스
- Exp. Mol. Med.
- 2025.01.13
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Comparison of thrombotic adverse events in patients treated with factor VIII products and emicizumab using the 2018-2022 FAERS data
- J. Thromb. Haemost. Feb 21 2024, S1538-7836(24)00109-0 | https://doi.org/10.1016/j.jtha.2024.02.009
- 2024.02
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In vivo genome editing for hemophilia B therapy by the combination of rebalancing and therapeutic gene knockin using a viral and non-viral vector
- Mol. Ther.-Nucl. Acids VOLUME 32, P161-172, JUNE 13, 2023 | https://doi.org/10.1016/j.omtn.2023.03.008
- 2023.06
- 생명과학
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Genome editing-mediated knock-in of therapeutic genes ameliorates the disease phenotype in a model of hemophilia
- Mol. Ther.-Nucl. Acids Available online 4 August 2022 | https://doi.org/10.1016/j.omtn.2022.08.002
- 2022.08
- 생명과학
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Therapeutic correction of hemophilia A using 2D endothelial cells and multicellular 3D organoids derived from CRISPR/Cas9-engineered patient iPSCs
- Biomaterials Volume 283, April 2022, 121429 | https://doi.org/10.1016/j.biomaterials.2022.121429
- 2022.04
- 생명과학
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In vivo delivery of CRISPR-Cas9 using lipid nanoparticles enables antithrombin gene editing for sustainable hemophilia A and B therapy
- Sci. Adv. 21 Jan 2022, Vol 8, Issue 3 | DOI: 10.1126/sciadv.abj6901
- 2022.01
- 의약학
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In vivo delivery of CRISPR-Cas9 using lipid nanoparticles enables antithrombin gene editing for sustainable hemophilia A and B therapy
- Sci. Adv. 21 Jan 2022, Vol 8, Issue 3 | DOI: 10.1126/sciadv.abj6901
- 2022.01
- 의약학
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한정필
서울대학교
- Sci. Adv.
- 2022.01.28
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FVIII-specific human chimeric antigen receptor T-regulatory cells suppress T- and B-cell responses to FVIII
- Blood January 12, 2017, 129(2):238-245 | doi: https://doi.org/10.1182/blood-2016-07-727834
- 2017.01
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Modeling and correction of structural variations in patient-derived iPSCs using CRISPR/Cas9
- Nat. Protoc. Published online 06 October 2016, 11, 2154-2169 | doi:10.1038/nprot.2016.129
- 2016.10
- 의약학
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Genome Editing of Structural Variations: Modeling and Gene Correction
- Trends Biotechnol. Published Online: March 22, 2016 | DOI: http://dx.doi.org/10.1016/j.tibtech.2016.02.011
- 2016.03
- 의약학
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박철용
연세대학교 의과대학
- Cell Stem Cell
- 2015.08.03
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Functional Correction of Large Factor VIII Gene Chromosomal Inversions in Hemophilia A Patient-Derived iPSCs Using CRISPR-Cas9
- Cell Stem Cell Volume 17, Issue 2, p213–220, 6 August 2015. Available online 23 July 2015 | doi:10.1016/j.stem.2015.07.001
- 2015.07
- 생명과학
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Functional Correction of Large Factor VIII Gene Chromosomal Inversions in Hemophilia A Patient-Derived iPSCs Using CRISPR-Cas9
- Cell Stem Cell Volume 17, Issue 2, p213–220, 6 August 2015. Available online 23 July 2015 | doi:10.1016/j.stem.2015.07.001
- 2015.07
- 생명과학
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Targeted inversion and reversion of the blood coagulation factor 8 gene in human iPS cells using TALENs
- Proc. Natl. Acad. Sci. USA published ahead of print June 9, 2014, doi:10.1073/pnas.1323941111
- 2014.06
- 의약학
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Oral delivery of human biopharmaceuticals, autoantigens and vaccine antigens bioencapsulated in plant cells
- Adv. Drug Deliv. Rev. Available online 23 October 2012 | http://dx.doi.org/10.1016/j.addr.2012.10.005
- 2012.10
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Targeted chromosomal duplications and inversions in the human genome using zinc finger nucleases
- Genome Res. Published in Advance December 19, 2011, doi: 10.1101/gr.129635.111
- 2011.12
- 생명과학
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Targeted chromosomal duplications and inversions in the human genome using zinc finger nucleases
- Genome Res. Published in Advance December 19, 2011, doi: 10.1101/gr.129635.111
- 2011.12
- 생명과학
